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Results for Rare diseases

Publications & Outputs

  1. Rare Disease Trials: Beyond the Randomised Controlled Trial

    Jackson, H., 2023, Lancaster University. 237 p.

    Research output: ThesisDoctoral Thesis

  2. A Bayesian adaptive design for clinical trials in rare diseases

    Williamson, F., Jacko, P., Villar, S. S. & Jaki, T. F., 09/2017, In: Computational Statistics and Data Analysis. 113, p. 136-153 17 p.

    Research output: Contribution to Journal/MagazineJournal articlepeer-review